Clinical trials: Progeria, open to volunteers
Progeria
Phase I/II Trial of Everolimus in Combination With Lonafarnib in Progeria
This is a phase I/II dose-escalation trial of everolimus in combination with lonafarnib in Hutchinson-Gilford Progeria Syndrome (HGPS) and progeroid laminopathies (henceforth "progeria").
- Trial name
- NCT02579044
- Testing
- Everolimus and lonafarnib
- Where
- United States
- Volunteers
- 80 people
- Sponsor
- Boston Children's Hospital
Hutchinson-Gilford Progeria Syndrome
A Study Observing Disease Progression in a Patient With Hutchinson-Gilford Progeria Syndrome (HGPS)
This study is a prospective, non-interventional, single-patient observational study following one patient with Hutchinson-Gilford Progeria Syndrome (HGPS), a rare disease that causes rapid, premature aging, over a 3-year period…
- Trial name
- progeria (NCT07839351)
- Where
- South Korea
- Volunteers
- 1 people
- Sponsor
- Bundang CHA Hospital
Hutchinson-Gilford Progeria Syndrome
Creating Stem Cells From a Progeria Patient's Blood to Test Candidate Treatments in the Lab
This study aims to establish induced pluripotent stem cell (iPSC) lines from the blood of one pediatric patient with Hutchinson-Gilford Progeria Syndrome (HGPS), a rare disease that causes rapid, premature aging, in order to…
- Trial name
- NCT07803432
- Volunteers
- 1 people
- Sponsor
- Bundang CHA Hospital