Clinical trials: Cystinuria
Cystinuria
Effect of Increasing Doses of Tiopronin on Cystine Capacity in Patients With Cystinuria
The purpose of this study is to determine the minimum effective dose of the cysteine binding thiol drug (CBTD) Tiopronin on urine cystine capacity, which is a measure of cystine solubility in the urine, in patients with…
- Trial name
- NCT03663855
- Testing
- Tiopronin
- Where
- United States
- Volunteers
- 10 people
- Sponsor
- NYU Langone Health
Cystinuria
Study Evaluating Patients With Cystinuria
This is an open label, multicentre study, evaluating the safety, tolerability, efficacy, compliance and acceptability of alkalising treatments at long-term in patients with cystinuria.
- Trial name
- NCT04137978
- Testing
- ADV7103, Standard of Care
- Where
- 13 sites in Belgium, France
- Sponsor
- Advicenne Pharma
Adenine Phosphoribosyltransferase Deficiency, AH Amyloidosis
National Registry of Rare Kidney Diseases
The goal of this National Registry is to is to collect information from patients with rare kidney diseases, so that it that can be used for research.
- Conditions
- Adenine Phosphoribosyltransferase Deficiency, AH Amyloidosis, AHL Amyloidosis, AL Amyloidosis
- Trial name
- RaDaR (NCT06065852)
- Where
- United Kingdom
- Volunteers
- 35,000 people
- Sponsor
- UK Kidney Association
Cystinuria
Study Evaluating Patients With Cystinuria and Efficacy and Safety Exploratory Study in the Youngest Children
This is a multicenter, randomized, controlled versus placebo, double-blinded, 4 parallel arms, dose-ranging main study, to evaluate the efficacy, safety and tolerability, and acceptability of repeated doses of ADV7103, after 7…
- Trial name
- NCT04147871
- Testing
- ADV7103
- Where
- 12 sites in Belgium, France
- Sponsor
- Advicenne Pharma