AzTrials
AzTrials

Familial HypercholesterolemiaNCT07653555

Cascade Testing In Identifying At-risk Family Members Of Individuals With Familial Hypercholesterolemia (FH) In PCP

A study testing Cascade testing in people with Familial Hypercholesterolemia, run by Mayo Clinic at 1 site in United States.

Not yet recruiting

Opening soon. The study is approved but enrolment has not started yet. Sites may already take enquiries.

Sites and contacts
Official record
Search all trials

Trial summary

The purpose of this study is to evaluate the effectiveness of two models of cascade testing in identifying at-risk family members of individuals diagnosed with familial hypercholesterolemia (FH). Read more about this study

Who is it for?
Ages 1 year and older
Conditions the study is for
Familial Hypercholesterolemia
What is being tested?
Cascade testing
Could I receive a placebo?
No, everyone receives an active treatment
How many people
480 participants
Where
1 siteUnited States
Study dates
20 Oct 2026to 20 Sep 2029
Phase
Interventional
Are there results?
Not yet: the study is under way

Key requirements

Who can take part, as listed by the sponsor. Only the study team can confirm whether you are eligible, so take this list to your doctor.

  • Ages 1 year and older
  • All sexes
  • No healthy volunteers
  • Child, Adult, Older adult

Who may be able to join

  • Index Patients:
  • Age ≥ 18 years.
  • Confirmed FH diagnosis using Dutch Lipid Clinic Network criteria *or* genetic confirmation.
  • Identified through REP or Tapestry databases.
  • Able and willing to provide informed consent.
  • At least one eligible first- or second-degree relative.
Show all 12Show fewer
  • Access to and active use of email (computer literacy requirement).
  • Relatives:
  • First- or second-degree relative of an enrolled index patient.
  • Age ≥ 1 year (minors require parental consent + assent).
  • Willing to participate and able to complete electronic consent (guardian-assisted if minor).
  • Access to and active use of email (guardian).

Who cannot join

  • Index Patients:
  • No confirmed FH diagnosis.
  • Insufficient clinical follow-up (<5 years).
  • No identifiable or contactable relatives.
  • Prior participation in structured cascade testing.
  • Severe cognitive impairment preventing informed consent.
Show all 9Show fewer
  • Relatives:
  • Prior participation in structured cascade testing.
  • Severe cognitive impairment preventing informed consent.

Trial locations and contacts

1 site in 1 country. Contact the study team or a site near you to ask about taking part.

Family Medicine Research Study Coordinators contact

507-422-6823

RSTFMSC@mayo.edu

United States1 site
  • Mayo Clinic in Rochester

    Rochester, Minnesota, 55905

    Family Medicine Research Study Coordinators, 507-422-6823, RSTFMSC@mayo.edu

    Elisa J. Houwink, MD, PhD

Other trials in United States

About this study

Official title: A Cluster Randomized Controlled Trial To Evaluate The Efficacy Of Cascade Testing In Identifying At-risk Family Members Of Individuals With Familial Hypercholesterolemia (FH) In PCP

The purpose of this study is to evaluate the effectiveness of two models of cascade testing in identifying at-risk family members of individuals diagnosed with familial hypercholesterolemia (FH).

Read the detailed description
  1. Index Patient Genetic Testing (only index patients from the REP database):
  • Index patients identified through the REP database will undergo confirmatory FH testing HCHLG panel
  • A sputum collection kit is mailed to participants along with a pre-addressed return mailer.
  • Results are recorded in the electronic medical record and communicated to index (REP) participants with next-step instructions.
  • Only index patients with confirmed pathogenic/likely pathogenic variants proceed in the study.
  1. Relative Genetic Testing:
  • Relatives in the intervention arm who contact the study team and consent will be mailed a Focused Molecular Targeted Test (FMTT) sputum kit.
  • Testing targets the specific FH variant identified in the corresponding index patient.
  • Testing costs are covered only for relatives in the intervention arm.
  • Control arm relatives may choose to pursue clinical genetic testing independently through their primary care provider referring them to genetic counselling (usual care).
  1. Baseline Data Collection (Index Patients):
  • Collection of demographics and FH-related history via REDCap.
  • LDL-C values abstracted from EMR; ROI used if external records are required.
  1. Randomization:
  • Index patients randomized 2:1 to intervention or control arm.
  • Randomization occurs only after completion of baseline survey.
  1. Intervention Arm Procedures: Indirect contact: In the CASCADE-FH trial, index patients receive IRB-approved recruitment letters, with contact information for the primary care study team, to distribute to up to three first- or second-degree relatives. Relatives who contact the team undergo screening and electronic consent. In this study, index patients choosing the indirect pathway are provided with structured Mayo approved educational materials to support the index patient in accurate and consistent communication with relatives. Direct Contact: In the CASCADE-FH trial, modified direct contact is operationalized through an IRB approved recruitment letter sent by the index patient to their relatives with contact information for the primary care study team. No direct outreach from the study team occurs unless a relative independently initiates contact to the study team. Relatives who contact the team undergo screening and electronic consent. After consent the primary care study team will be able to provide direct support to the at-risk relatives, provide Mayo-approved patient educational materials, and inform them of their potential risk for FH and the opportunity for genetic testing. This approach allows the primary care study team to provide a more direct method of communication and interaction with the at-risk relatives. The study team will also facilitate genetic testing, should the relative wish to proceed with genetic testing for FH.
  • Intervention-arm relatives receive FMTT sputum kits paid for by the study.
  1. Control Arm Procedures:
  • Index patients receive usual care. No structured outreach is provided.
  • Relatives may seek genetic testing for FH through their primary care provider referring them to genetic counselling.
  • The study does not cover genetic counseling or testing costs in the control arm.
  1. Relative Procedures (All Arms):
  • Relatives who contact the research team receive full study information and undergo screening and consent.
  • Baseline surveys collected via REDCap.
  • Minors require parental consent and age-appropriate assent.
  1. Follow-Up Surveys:
  • Index patients and relatives receive surveys at 1, 3, and 12 months via REDCap.
  • Up to two reminder emails are sent approximately 7 days apart.
  • Participants who do not respond after reminders are classified as lost to follow-up.
  1. Genetic Testing Workflow:
  • Returned sputum kits will be processed.
  • Results entered into EMR for all participants.
  • index (REP) participants and relatives in the intervention arm are notified via secure message or email on next steps.
  • Index (REP) participants who test positive are instructed to follow up with their primary care provider.
  • Follow-up for Positive Findings for Relatives in the intervention arm:

Participants who receive a pathogenic or likely pathogenic result for FH will be notified via secure patient portal or email. Notifications will instruct the participant to contact their primary care provider for referral to genetic counseling and/or preventive cardiology.

Parents or guardians of minors aged 1-18 years who test positive will be instructed to contact the child's primary care provider to obtain referral to a pediatric endocrinologist.

Being tested
Cascade testing, Standard of Care
Medical subject headings
Hyperlipoproteinemia Type II

What participants receive

What participants receive. In a randomised study each person is assigned to one group by chance.

  • Cascade testingOther

    Patient relatives will be contacted either directly or indirectly per patient preference:

    The indirect contact method provides patients with structured Mayo approved educational materials to support the index patient in accurate and consistent communication with relatives. Relatives have the option to contact the study team for cascade genetic testing.

    The direct contact method provides patients with a letter inviting relatives to contact the study team. After contact, relatives are offered educational materials and the opportunity for cascade genetic testing.

  • Standard of CareOther

    No structured outreach is provided to patient or family members. Relatives may have their primary care provider refer them to genetic counseling services for cascade testing coordination.

Study groups in NCT07653555
Study groupRoleWhat they receive
Usual CareActive comparatorPatients will receive standard of care support
Receives: Other: Standard of Care
Structured OutreachExperimentalPatients and relatives will receive outreach in the form of direct or indirect contact
Receives: Other: Cascade testing

What is being measured

The primary outcome is the main question the study is designed to answer.

  1. Genetic testing among first- and second-degree relatives within 12 months of index patient enrollment

    Defined as total number of relations to complete CLIA-certified FH test (LDLR, APOB, PCSK9, LDLRAP1) with result returned to the primary care research team.

    Measured: 2 year

Secondary outcomes (6)
  1. Number of newly diagnosed FH cases among relatives

    Total number of patient relatives newly diagnosed with familial hypercholesterolemia (FH)

    Measured: 2 years

  2. Time from index patient enrollment (Tapestry identified participants) and diagnosis (REP identified and FH genetic test confirmation) to relative testing

    Number of days between patient enrollment and testing of relatives

    Measured: 2 years

  3. Time from relative diagnosis to treatment initiation

    Number of days between diagnosis and start of treatment

    Measured: 2 years

  4. Communication modality preference

    letter sent by the index patient to their relatives with contact information for the primary care study team. the indirect pathway are provided with structured Mayo approved educational materials to support the index patient in accurate and consistent communication with relatives.

    Measured: 2 years

  5. Referral completion (genetics, cardiology, preventive cardiology) within 6 months of positive result

    Number of patients to be referred to specialty within 6 months of positive result

    Measured: 2 years

  6. Cascade depth (degree of relatives reached)

    Degree of relatives reached (1st, 2nd, 3rd)

    Measured: 2 years

Timeline

From the start of the study to its completion; the mark is today. Estimated dates are the sponsor’s plan.

  1. First posted17 Jun 2026
  2. Study start20 Oct 2026 (estimated)
  3. Primary completion20 Jun 2028 (estimated)
  4. Study completion20 Sep 2029 (estimated)

Resources

More details

For doctors and researchers: how the study is designed, who runs it, and its registry IDs.

Study design
Study type
Interventional
Phase
Phase N/A
Primary purpose
Other
Allocation
Randomised
Intervention model
Parallel groups
Masking
None (open label)
Enrolment
480 participants (estimated)
IDs, dates and publications
ClinicalTrials.gov ID
NCT07653555
Sponsor's protocol ID
26-001620
Status last verified
Sep 2026
First submitted
2 Jun 2026
Last updated
18 Sep 2026
Results posted
No
Data monitoring committee
No
FDA-regulated drug
No
FDA-regulated device
No
Individual data sharing
No

Questions about this trial

What is this clinical trial studying?

A study testing Cascade testing in people with Familial Hypercholesterolemia, run by Mayo Clinic at 1 site in United States.

The full registered description is in the About this study section and the official record.

Who may be eligible to take part?

The sponsor lists 12 inclusion and 9 exclusion criteria. Eligibility is decided by the study team after screening, so read the full criteria and contact a listed site.

Is this clinical trial currently recruiting?

The record says: opening soon, as of the sponsor's last update on 18 Sep 2026. Status can change between updates, so confirm with the study contact before making plans.

Where is the study taking place?

The record lists 1 site in United States. Whether a site is taking part right now should be confirmed with that site. See every site.

What are the possible benefits and risks?

They depend on the study and the treatment, and no study can promise a benefit. The study team explains the known risks during informed consent, before anyone joins; the record itself does not list them.

Are results available for this study?

This study is still under way. Results are not available in the source record yet.

How can a doctor refer a patient or contact the research team?

Contact Family Medicine Research Study Coordinators (507-422-6823, RSTFMSC@mayo.edu), or a site near the patient. AzTrials does not enrol participants or take referrals.

What does the primary outcome measure?

Genetic testing among first- and second-degree relatives within 12 months of index patient enrollment (time frame: 2 year). It is what the study was designed to measure, not a finding.

Where can I read the original study information?
Does a listing mean the treatment is approved or proven to work?

No. A listing means the study is registered. It does not show that the treatment is safe, works, or is approved by a regulator.

How often is this information updated?

AzTrials copies changed records from ClinicalTrials.gov every night and reloads the whole registry every week. The sponsor last updated this record on 18 Sep 2026.

Free account

Log in to keep searching

You’ve used your 3 free searches. AzTrials is free: log in or create a free account to keep searching clinical trials and save the ones you want to follow.

Create a free accountLog in