TuberculosisNCT01687504
Pharmacokinetics of Anti-TB Drugs in HIV/TB Co-infected Children in Ghana
An observational study of Tuberculosis and HIV, run by The Miriam Hospital at 1 site in Ghana.
Trial summary
Tuberculosis (also known as TB) is a common infection and a major cause of death in children. Effective treatment using a combination of anti-tuberculosis (anti-TB) medications saves lives, but dosages of these medications are not well established in children. Read more about this study
- Who is it for?
- Ages 3 months to 14 years
- Conditions the study is for
- Tuberculosis, HIV
- How many people
- 106 participants
- Where
- 1 siteGhana
- Study dates
- Oct 2012to May 2017
- Phase
- Observational
- Are there results?
- None posted in the registry
Key requirements
Who can take part, as listed by the sponsor. Only the study team can confirm whether you are eligible, so take this list to your doctor.
- Ages 3 months to 14 years
- All sexes
- No healthy volunteers
- Child
Study population: Children aged 3 months to 14 years old with active tuberculosis with or with HIV coinfection
Who may be able to join
- Children with active TB with or without HIV co-infection. Active TB diagnosis defined by clinical criteria consistent with active TB and/or a positive AFB smear or mycobacterial culture.
- Aged 3 months to 14 years old.
- Available for follow-up until completion of TB treatment and/or achievement of a study endpoint like discontinuation of therapy, and/or pharmacokinetic sampling.
Who cannot join
- Unable to obtain informed signed consent parent(s) or legal guardian.
- Have AIDS-related opportunistic infections other than TB, history of or proven acute hepatitis within 30 days of study entry, persistent vomiting, or diarrhea.
- Hemoglobin < 6 g/dl, white blood cells < 2500/mm3, serum creatinine > 1.5 mg/dl, AST and ALT > 2X upper limit of normal.
Trial locations and contacts
1 site in 1 country.
Ghana1 site, 1 recruiting
- Recruiting
Komfo Anokye Teaching Hospital
Kumasi
Sampson Antwi, MBChB, +233265812061, antwisampson@yahoo.com
Anthony Enimil, MBChB, +233208164433, tenimil@live.com
About this study
Official title: Pharmacokinetics and Safety of the WHO Recommended Increased Dosages of the First-line Anti-TB Medications in Children With TB and HIV/TB Coinfection
Tuberculosis (also known as TB) is a common infection and a major cause of death in children. Effective treatment using a combination of anti-tuberculosis (anti-TB) medications saves lives, but dosages of these medications are not well established in children. Several research studies have shown that the recommended dosages of the anti-TB medications in children do not lead to adequate blood levels to kill the bacteria in some children. This situation may lead to treatment failure and emergence of drug resistance. As a result, the world Health Organization (WHO) recently recommended increased dosages for all the TB medications in children. This study is being conducted to find out if the increased dosages of the anti-TB drugs are safe and lead to adequate drug levels in the blood of children with TB with or without HIV infection.
Read the detailed description
The treatment guidelines for childhood TB are largely inferred from studies in adults, as few controlled trials have been done in children to establish optimum regimens. The standard anti-TB treatment consists of a combination of isoniazid, rifampin, pyrazinamide and ethambutol for two months induction phase followed by 2 months of isoniazid and rifampin in the continuation phase. The plasma and tissue concentrations of each of the drugs in the combination regimen needs to be optimized to maximize bacterial killing and reduce the risk of treatment failure with emergence of drug resistance. Several studies have shown that the peak concentrations of these drugs in a large proportion of children are so low that there is a concern for ineffective therapy in some children. This concern led to the recent recommendation by the WHO to increase the dosages of all first-line anti-TB drugs in children. To our knowledge, the safety and pharmacokinetics of the new dosages have not been studied in children in West Africa. In addition, differences in drug absorption, metabolism and excretion may put some children at risk of low drug concentrations when the standard weight-based fixed-dosages are prescribed to all children. Identification of these individuals clinically or through genetic testing may be important for individualized dosing. The factors that may influence drug concentrations and treatment effects include age, HIV coinfection status, nutritional status and genetic polymorphisms of drug metabolizing enzymes and transporters. Younger children appear to eliminate the drugs faster and have lower plasma peak concentrations compared to older children and adults treated with similar mg/kg doses. The association between nutritional status and the plasma pharmacokinetics of the anti-TB drugs is less clear, as some but not all studies report a significant relationship. HIV coinfection is an important factor that has been associated with poor treatment responses as a result of poor drug absorption.
The primary objective of this study is to evaluate the pharmacokinetics and tolerability of the elevated dosages of the first-line anti-TB in children, as well as factors associated with inter-individual variability in anti-TB drugs exposure in Ghanaian children.
A two-arm pharmacokinetic study in children with active TB with or without HIV coinfection will be performed at Komfo Anokye Teaching Hospital, Kumasi, Ghana. Children aged between 3 months and 14 years, for whom informed consent by parent or guardian have been obtained, will be enrolled. A complete medical history, physical examination, and nutritional status assessment will be performed at enrolment at subsequent study visits. Relevant data will be collected using standardized forms. Baseline measurements prior to initiation of anti-TB treatment will include complete blood count (CBC), blood urea nitrogen, creatinine, liver function tests (LFTs), as well as CD4 cell count determination and plasma HIV-1 RNA level (if HIV co-infected). Measurements LFTs will be repeated at week 2 of therapy or when clinically indicated to evaluate for drug toxicity. All study participants will follow-up at 2 and 4 weeks and then monthly to assess adverse events and clinical response to therapy.
Anti-TB treatment will be initiated immediately upon TB diagnosis and concurrent initiation ART will be allowed in co-infected children as per national and WHO guidelines. The standard anti-TB regimen consists of daily ingestion of isoniazid, rifampin, pyrazinamide and ethambutol for 2 months, then rifampin and isoniazid daily for 4 months. The new WHO recommended doses for children will be prescribed. Weight-based fixed-dose combination tablets are used. Children will receive directly observed therapy for the anti-TB treatment by healthcare worker at the hospital or family member at home. Treatment outcome (completed/cured, died, defaulted, discontinued, transferred out) is defined according to WHO criteria.
Pharmacokinetic sampling will be performed at 4 weeks of anti-TB therapy. Study drugs will be administered after at least a 2-hour fast in non-breastfed children and blood samples obtained through intravascular catheters at times 0, 2, 4, 6, 8-hours post dosing. Actual times of dosing and sampling will be accurately recorded. Doses vomited < 30 minutes after dosing will require cancellation of PK testing and rescheduling. The samples will be placed immediately on ice and centrifuged within 30 minutes at 3000g for 10 minutes at 4oC. Plasma will be stored at - 70oC until measurement of drug concentrations. Drug concentrations will be determined using validated gas chromatography with mass spectrometry.
- Conditions
- Tuberculosis, HIV
- Keywords
- pharmacokinetics, children, HIV, Tuberculosis, Pharmacogenetics
- Medical subject headings
- Tuberculosis
What is being measured
The primary outcome is the main question the study is designed to answer.
Descriptive statistics of PK parameters (Cmax, Tmax, AUC0-8h) of rifampin, isoniazid, pyrazinamide and ethambutol in children with TB with and without HIV coinfection
Measured: Week 4 of therapy
Secondary outcomes (6)
Frequency of liver enzymes elevations compare to baseline, skin rashes, nausea, vomiting and treatment discontinuation or modifications due to drug side effects in children with TB with and without HIV coinfection
The frequency of each drug side effects between children with TB and children with with HIV/TB confection on standard anti-TB therapy will be compared by chi-square test
Measured: up to week 24
Relationship between genetic polymorphisms of N-acetyltransferase type 2 (NAT2) enzyme and isoniazid plasma Cmax and AUC in Ghanaian children with TB with and without HIV
Genetic effect of each genetic variant on PK parameter will be estimated as odds ratio between carrier and non-carrier for each variant
Measured: Week 4 of therapy
Relationship between genetic polymorphisms of SLCO1B1 transporter and rifampin plasma Cmax and AUC in Ghanaian children with TB with and without HIV
Genetic effect of each genetic variant on PK parameter will be estimated as odds ratio between carrier and non-carrier for each genetic variant
Measured: week 4 of therapy
Relationship between plasma Cmax and AUC of isoniazid, rifampin, ethambutol and pyrazinamide at week 4 of therapy and frequency of anti-TB treatment discontinuation or modification
Differences in mean Cmax and AUC of each drug between children who complete 6 months anti-TB therapy and those who require treatment modification due to drug side effects will be compared by t-test or non-parametric test. Note that treatment modification due to drug side effects is as per national TB treatment guidelines but no new interventions are prescribed in this observation study.
Measured: up to week 24
Relationship between NAT2 acelator status, SLCO1B1 genotype status and anti-TB treatment completion, discontinuation or modification
Genetic effect of each genetic variant on treatment discontinuation or modification rates will be estimated as odds ratio between carrier and non-carrier for each variant. Note that treatment modification due to drug side effects is as per national TB treatment guidelines but no new interventions are prescribed in this observation study.
Measured: up to week 24
Relationship between body weight, gender, nutritional status and plasma Cmax and AUC of isoniazid, rifampin, ethambutol and pyrazinamide in Ghanaian children with TB with and without HIV
Appropriate regression model will be used to test correlation between clinical factors and anti-TB drugs PK parameters
Measured: up to week 4 of therapy
Timeline
From the start of the study to its completion; the mark is today. Estimated dates are the sponsor’s plan.
- First posted19 Sep 2012 (estimated)
- Study startOct 2012
- Primary completionMay 2017 (estimated)
- Study completionMay 2017 (estimated)
Resources
- Official record on ClinicalTrials.govThe registry entry this page is built from, with its full change history.
- Publications (2)Papers the sponsor has linked to this study.
- Other trials for TuberculosisStudies of the same condition, open and under way.
- What the trial phases meanHow a treatment moves from first tests in people to approval.
More details
For doctors and researchers: how the study is designed, who runs it, and its registry IDs.
Study design
- Study type
- Observational
- Observational model
- Cohort
- Time perspective
- Prospective
- Enrolment
- 106 participants (estimated)
Sponsor and investigators
- Lead sponsor
- The Miriam Hospital
- Sponsor type
- University, hospital or other
- Collaborators
- Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)
- Responsible party
- Sponsor
- Investigators
- Awewura Kwara, MD, MPH&TM, Principal investigator, The Miriam Hospital
IDs, dates and publications
- ClinicalTrials.gov ID
- NCT01687504
- Sponsor's protocol ID
- PK-PTBHIV01
- Other IDs
- R01HD071779
- Status last verified
- Sep 2012
- First submitted
- 11 Sep 2012
- Last updated
- 11 Oct 2012
- Results posted
- No
- Data monitoring committee
- Yes
Publications
Horita Y, Alsultan A, Kwara A, Antwi S, Enimil A, Ortsin A, Dompreh A, Yang H, Wiesner L, Peloquin CA. Evaluation of the Adequacy of WHO Revised Dosages of the First-Line Antituberculosis Drugs in Children with Tuberculosis Using Population Pharmacokinetic Modeling and Simulations. Antimicrob Agents Chemother. 2018 Aug 27;62(9):e00008-18. doi: 10.1128/AAC.00008-18. Print 2018 Sep.
PubMed 29914960Antwi S, Yang H, Enimil A, Sarfo AM, Gillani FS, Ansong D, Dompreh A, Orstin A, Opoku T, Bosomtwe D, Wiesner L, Norman J, Peloquin CA, Kwara A. Pharmacokinetics of the First-Line Antituberculosis Drugs in Ghanaian Children with Tuberculosis with or without HIV Coinfection. Antimicrob Agents Chemother. 2017 Jan 24;61(2):e01701-16. doi: 10.1128/AAC.01701-16. Print 2017 Feb.
PubMed 27855070
Study at a glance
From the registry record, last updated by the sponsor on 11 Oct 2012. Recruitment status is as the sponsor reported it: confirm with the study team.
- Official title
- Pharmacokinetics and Safety of the WHO Recommended Increased Dosages of the First-line Anti-TB Medications in Children With TB and HIV/TB Coinfection
- ClinicalTrials.gov ID
- NCT01687504
- Acronym / sponsor ID
- PK-PTBHIV01
- Conditions
- Tuberculosis, HIV
- Keywords
- pharmacokinetics, children, HIV, Tuberculosis, Pharmacogenetics
- Study type
- Observational
- Recruitment status
- Unknown status
- Enrolment
- 106 participants (estimated)
- Lead sponsor
- The Miriam HospitalUniversity, hospital or other
- Collaborators
- Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)
- Study start
- Oct 2012
- Primary completion
- May 2017 (estimated)
- Study completion
- May 2017 (estimated)
- First posted
- 19 Sep 2012 (estimated)
- Results
- Not posted in the source record
Clinical summary
The research question as the sponsor registered it. This describes what the study plans to test, not what it found.
Tuberculosis (also known as TB) is a common infection and a major cause of death in children. Effective treatment using a combination of anti-tuberculosis (anti-TB) medications saves lives, but dosages of these medications are not well established in children. Several research studies have shown that the recommended dosages of the anti-TB medications in children do not lead to adequate blood levels to kill the bacteria in some children. This situation may lead to treatment failure and emergence of drug resistance. As a result, the world Health Organization (WHO) recently recommended increased dosages for all the TB medications in children. This study is being conducted to find out if the increased dosages of the anti-TB drugs are safe and lead to adequate drug levels in the blood of children with TB with or without HIV infection.
Detailed description
The treatment guidelines for childhood TB are largely inferred from studies in adults, as few controlled trials have been done in children to establish optimum regimens. The standard anti-TB treatment consists of a combination of isoniazid, rifampin, pyrazinamide and ethambutol for two months induction phase followed by 2 months of isoniazid and rifampin in the continuation phase. The plasma and tissue concentrations of each of the drugs in the combination regimen needs to be optimized to maximize bacterial killing and reduce the risk of treatment failure with emergence of drug resistance. Several studies have shown that the peak concentrations of these drugs in a large proportion of children are so low that there is a concern for ineffective therapy in some children. This concern led to the recent recommendation by the WHO to increase the dosages of all first-line anti-TB drugs in children. To our knowledge, the safety and pharmacokinetics of the new dosages have not been studied in children in West Africa. In addition, differences in drug absorption, metabolism and excretion may put some children at risk of low drug concentrations when the standard weight-based fixed-dosages are prescribed to all children. Identification of these individuals clinically or through genetic testing may be important for individualized dosing. The factors that may influence drug concentrations and treatment effects include age, HIV coinfection status, nutritional status and genetic polymorphisms of drug metabolizing enzymes and transporters. Younger children appear to eliminate the drugs faster and have lower plasma peak concentrations compared to older children and adults treated with similar mg/kg doses. The association between nutritional status and the plasma pharmacokinetics of the anti-TB drugs is less clear, as some but not all studies report a significant relationship. HIV coinfection is an important factor that has been associated with poor treatment responses as a result of poor drug absorption.
The primary objective of this study is to evaluate the pharmacokinetics and tolerability of the elevated dosages of the first-line anti-TB in children, as well as factors associated with inter-individual variability in anti-TB drugs exposure in Ghanaian children.
A two-arm pharmacokinetic study in children with active TB with or without HIV coinfection will be performed at Komfo Anokye Teaching Hospital, Kumasi, Ghana. Children aged between 3 months and 14 years, for whom informed consent by parent or guardian have been obtained, will be enrolled. A complete medical history, physical examination, and nutritional status assessment will be performed at enrolment at subsequent study visits. Relevant data will be collected using standardized forms. Baseline measurements prior to initiation of anti-TB treatment will include complete blood count (CBC), blood urea nitrogen, creatinine, liver function tests (LFTs), as well as CD4 cell count determination and plasma HIV-1 RNA level (if HIV co-infected). Measurements LFTs will be repeated at week 2 of therapy or when clinically indicated to evaluate for drug toxicity. All study participants will follow-up at 2 and 4 weeks and then monthly to assess adverse events and clinical response to therapy.
Anti-TB treatment will be initiated immediately upon TB diagnosis and concurrent initiation ART will be allowed in co-infected children as per national and WHO guidelines. The standard anti-TB regimen consists of daily ingestion of isoniazid, rifampin, pyrazinamide and ethambutol for 2 months, then rifampin and isoniazid daily for 4 months. The new WHO recommended doses for children will be prescribed. Weight-based fixed-dose combination tablets are used. Children will receive directly observed therapy for the anti-TB treatment by healthcare worker at the hospital or family member at home. Treatment outcome (completed/cured, died, defaulted, discontinued, transferred out) is defined according to WHO criteria.
Pharmacokinetic sampling will be performed at 4 weeks of anti-TB therapy. Study drugs will be administered after at least a 2-hour fast in non-breastfed children and blood samples obtained through intravascular catheters at times 0, 2, 4, 6, 8-hours post dosing. Actual times of dosing and sampling will be accurately recorded. Doses vomited < 30 minutes after dosing will require cancellation of PK testing and rescheduling. The samples will be placed immediately on ice and centrifuged within 30 minutes at 3000g for 10 minutes at 4oC. Plasma will be stored at - 70oC until measurement of drug concentrations. Drug concentrations will be determined using validated gas chromatography with mass spectrometry.
Study design
- Observational model
- Cohort
- Time perspective
- Prospective
Who may qualify
- Ages
- 3 months to 14 years
- Sex
- All
- Healthy volunteers
- Not accepted
- Age groups
- Child
- Study population
- Children aged 3 months to 14 years old with active tuberculosis with or with HIV coinfection
Key inclusion criteria (3 listed)
- Children with active TB with or without HIV co-infection. Active TB diagnosis defined by clinical criteria consistent with active TB and/or a positive AFB smear or mycobacterial culture.
- Aged 3 months to 14 years old.
- Available for follow-up until completion of TB treatment and/or achievement of a study endpoint like discontinuation of therapy, and/or pharmacokinetic sampling.
Key exclusion criteria (3 listed)
- Unable to obtain informed signed consent parent(s) or legal guardian.
- Have AIDS-related opportunistic infections other than TB, history of or proven acute hepatitis within 30 days of study entry, persistent vomiting, or diarrhea.
- Hemoglobin < 6 g/dl, white blood cells < 2500/mm3, serum creatinine > 1.5 mg/dl, AST and ALT > 2X upper limit of normal.
Eligibility is decided by the study team after screening; this overview does not establish that a patient qualifies. Full inclusion and exclusion criteria.
Primary outcome
Descriptive statistics of PK parameters (Cmax, Tmax, AUC0-8h) of rifampin, isoniazid, pyrazinamide and ethambutol in children with TB with and without HIV coinfection
Time frame: Week 4 of therapy
6 secondary outcomes
Frequency of liver enzymes elevations compare to baseline, skin rashes, nausea, vomiting and treatment discontinuation or modifications due to drug side effects in children with TB with and without HIV coinfection
Time frame: up to week 24
Relationship between genetic polymorphisms of N-acetyltransferase type 2 (NAT2) enzyme and isoniazid plasma Cmax and AUC in Ghanaian children with TB with and without HIV
Time frame: Week 4 of therapy
Relationship between genetic polymorphisms of SLCO1B1 transporter and rifampin plasma Cmax and AUC in Ghanaian children with TB with and without HIV
Time frame: week 4 of therapy
Relationship between plasma Cmax and AUC of isoniazid, rifampin, ethambutol and pyrazinamide at week 4 of therapy and frequency of anti-TB treatment discontinuation or modification
Time frame: up to week 24
Relationship between NAT2 acelator status, SLCO1B1 genotype status and anti-TB treatment completion, discontinuation or modification
Time frame: up to week 24
Relationship between body weight, gender, nutritional status and plasma Cmax and AUC of isoniazid, rifampin, ethambutol and pyrazinamide in Ghanaian children with TB with and without HIV
Time frame: up to week 4 of therapy
Results and safety
Results are not available in the source record.
Research links
- Official record on ClinicalTrials.govLast updated by the sponsor 11 Oct 2012.
- Derived from this study: PubMed 29914960Horita Y, Alsultan A, Kwara A, Antwi S, Enimil A, Ortsin A, Dompreh A, Yang H, Wiesner L, Peloquin CA. Evaluation of the Adequacy of WHO Revised Dosages of the First-Line Antituberculosis Drugs in Children with Tuberculosis Using Population Pharmacokinetic Modeling and Simulations. Antimicrob Agents Chemother. 2018 Aug 27;62(9):e00008-18. doi: 10.1128/AAC.00008-18. Print 2018 Sep.
- Derived from this study: PubMed 27855070Antwi S, Yang H, Enimil A, Sarfo AM, Gillani FS, Ansong D, Dompreh A, Orstin A, Opoku T, Bosomtwe D, Wiesner L, Norman J, Peloquin CA, Kwara A. Pharmacokinetics of the First-Line Antituberculosis Drugs in Ghanaian Children with Tuberculosis with or without HIV Coinfection. Antimicrob Agents Chemother. 2017 Jan 24;61(2):e01701-16. doi: 10.1128/AAC.01701-16. Print 2017 Feb.
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Referral and contact
AzTrials does not enrol participants or take referrals. Contact the study team or a site listed below; they decide who can take part. This study is not recruiting at the moment.
Awewura Kwara, MD, MPH&TM principal investigator
The Miriam Hospital
1 site in 1 country: see every site and its status.
Questions about this trial
What is this clinical trial studying?
An observational study of Tuberculosis and HIV, run by The Miriam Hospital at 1 site in Ghana.
The full registered description is in the About this study section and the official record.
Who may be eligible to take part?
The sponsor lists 3 inclusion and 3 exclusion criteria. Eligibility is decided by the study team after screening, so read the full criteria and contact a listed site.
Is this clinical trial currently recruiting?
The record says: status not confirmed, as of the sponsor's last update on 11 Oct 2012. Status can change between updates, so confirm with the study contact before making plans.
Where is the study taking place?
The record lists 1 site in Ghana. Whether a site is taking part right now should be confirmed with that site. See every site.
What are the possible benefits and risks?
They depend on the study and the treatment, and no study can promise a benefit. The study team explains the known risks during informed consent, before anyone joins; the record itself does not list them.
Are results available for this study?
Results are not available in the source record.
How can a doctor refer a patient or contact the research team?
Contact Awewura Kwara, MD, MPH&TM (4017932463, akwara@lifespan.org), or a site near the patient. AzTrials does not enrol participants or take referrals.
What does the primary outcome measure?
Descriptive statistics of PK parameters (Cmax, Tmax, AUC0-8h) of rifampin, isoniazid, pyrazinamide and ethambutol in children with TB with and without HIV coinfection (time frame: Week 4 of therapy). It is what the study was designed to measure, not a finding.
Where can I read the original study information?
On the ClinicalTrials.gov record for NCT01687504, which also lists 2 linked publications.
Does a listing mean the treatment is approved or proven to work?
No. A listing means the study is registered. It does not show that the treatment is safe, works, or is approved by a regulator.
How often is this information updated?
AzTrials copies changed records from ClinicalTrials.gov every night and reloads the whole registry every week. The sponsor last updated this record on 11 Oct 2012.