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LeukemiaPhase 2NCT00003913

Umbilical Cord Blood Transplantation in Treating Patients With Hematologic Cancer or Nonmalignant Hematologic Disease

A Phase 2 study testing anti-thymocyte globulin, filgrastim and busulfan in people with Leukemia and Lymphoma, run by Fred Hutchinson Cancer Center at 23 sites in United States.

Completed

Finished. The study has ended and is not enrolling. Results may be posted on the official record.

Official record
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Trial summary

RATIONALE: Drugs used in chemotherapy use different ways to stop cancer cells from dividing so they stop growing or die. Umbilical cord blood transplantation may be able to replace immune cells that were destroyed by the chemotherapy or radiation therapy that was used to kill cancer cells. Read more about this study

Who is it for?
Ages Up to 18 years
Conditions the study is for
Leukemia, Lymphoma, Myelodysplastic Syndromes
What is being tested?
anti-thymocyte globulin, filgrastim and busulfan
Type of treatment
Surgery or procedure
How many people
390 participants
Where
23 sitesUnited States
Study dates
Dec 1998to Aug 2005
Phase
Phase 2
Are there results?
None posted in the registry

Key requirements

Who can take part, as listed by the sponsor. Only the study team can confirm whether you are eligible, so take this list to your doctor.

  • Ages Up to 18 years
  • All sexes
  • No healthy volunteers
  • Child, Adult

DISEASE CHARACTERISTICS:

  • One of the following diagnoses:
  • Acute myeloid leukemia (AML), with or without myelodysplastic syndromes
  • Not in first complete remission (CR)* with translocations t(8;21) and inv (16) unless failure of first-line induction therapy
  • Not in first CR* with translocations t(15;17) abnormality unless:
  • Failure of first-line induction therapy OR
  • Molecular evidence of persistent disease
  • Not in first CR with Down syndrome
  • Patients with third or greater medullary relapse or refractory disease (other than primary induction failures) receive busulfan/melphalan conditioning regimen NOTE: * CR defined by no greater than 5% blasts in marrow
  • Acute lymphocytic leukemia (ALL)
  • Not in first CR OR
  • High-risk ALL in first CR, with high risk defined as one of the following:
  • Hypoploidy (no greater than 44 chromosomes)
  • Pseudodiploidy with translocations or molecular evidence of t(9;22), 11q23, or t(8;14) (except B-cell ALL) with or without MLL gene arrangement
  • Elevated WBC at presentation
  • Age 6-12 months: greater than 100,000/mm^3
  • Age 10-17 years: greater than 200,000/mm^3
  • Age 18: greater than 20,000/mm^3
  • Failed to achieve CR after 4 weeks of induction therapy
  • Patients with B-ALL must not be in first CR, must meet at least one of the high-risk criteria specified above, or must not meet any of the following criteria:
  • Translocation t(8;14)
  • Blasts have surface immunoglobulins
  • CD10 positive
  • Patients with third or greater medullary relapse or refractory disease (other than primary induction failures) receive busulfan/melphalan conditioning regimen
  • Chronic myelogenous leukemia, meeting criteria for 1 of the following:
  • Accelerated phase
  • Chronic phase if 1 year from diagnosis without a matched unrelated bone marrow donor AND unresponsive to or unable to tolerate interferon
  • Blast crisis, defined as greater than 30% promyelocytes plus blasts in bone marrow
  • Patients receive busulfan/melphalan conditioning regimen
  • Acute undifferentiated leukemia (AUL), infant leukemia, or biphenotypic leukemia
  • Patients with third or greater medullary relapse or refractory disease (other than primary induction failures) receive busulfan/melphalan conditioning regimen
  • Juvenile myelomonocytic leukemia meeting the following criteria:
  • No Philadelphia chromosome
  • Bone marrow blasts less than 30%
  • Peripheral blood monocytes greater than 1,000/mm^3
  • At least 2 of the following:
  • Peripheral blood spontaneous growth and/or sargramostim (GM-CSF) hypersensitivity
  • Increased hemoglobin F for age
  • Clonal abnormalities (e.g., monosomy 7 or RAS mutations)
  • Peripheral blood with myeloid precursors
  • WBC greater than 10,000/mm^3
  • Myelodysplastic syndromes defined by the following:
  • Refractory anemia (RA)
  • RA with ringed sideroblasts
  • RA with excess blasts (RAEB)
  • RAEB in transformation
  • Chronic myelomonocytic leukemia
  • Paroxysmal nocturnal hemoglobinuria
  • Hodgkin's lymphoma or non-Hodgkin's lymphoma beyond first CR or primary induction failures AND chemosensitive (greater than 50% reduction in tumor mass size)
  • Inborn error of metabolism including, but not limited to, Hurler's syndrome, adrenoleukodystrophy (ALD), Maroteaux-Lamy syndrome, globoid cell leukodystrophy, metachromatic leukodystrophy, fucosidosis, or mannosidosis
  • For ALD patients over age 5, IQ must be at least 80
  • For all other patients over age 5, IQ must be at least 70
  • For all patients age 5 and under, developmental quotient or clinical neurodevelopmental examination should demonstrate potential for stabilization at a level of functioning where continuous life support (e.g., mechanical ventilation) would not be predicted to be required in the year after transplantation
  • Combined immune deficiencies including, but not limited to:
  • Severe combined immunodeficiency (SCID) requiring cytoreduction
  • Wiskott-Aldrich syndrome
  • Leukocyte adhesion defect
  • Chediak-Higashi disease
  • X-linked lymphoproliferative disease
  • Adenosine deaminase deficiency
  • Purine nucleoside phosphorylase deficiency
  • X-linked SCID
  • Common variable immune deficiency
  • Nezelof's syndrome
  • Cartilage hair hypoplasia
  • No dyskeratosis congenita
  • No ALL, AML, AUL, or biphenotypic leukemia in third or higher medullary relapse or refractory disease other than primary induction failure
  • No primary myelofibrosis or myelofibrosis grade 3 or worse
  • No active CNS leukemia involvement (CSF with WBC greater than 5/mm^3 and malignant cells on cytospin)
  • No consenting 5/6 or 6/6 HLA-matched related donor available
  • 3-6/6 HLA-matched unrelated umbilical cord blood donor available

PATIENT CHARACTERISTICS:

Age:

  • See Disease Characteristics
  • 18 and under

Performance status:

  • Karnofsky 70-100%, if age 16 to 18
  • Lansky 50-100%, if under age 16

Life expectancy:

  • Not specified

Hematopoietic:

  • See Disease Characteristics

Hepatic:

  • Bilirubin less than 2.5 mg/dL
  • SGOT less than 5 times upper limit of normal

Renal:

  • Creatinine normal for age OR
  • Creatinine clearance or glomerular filtration rate greater than 50% lower limit of normal for age

Cardiovascular:

  • If symptomatic:
  • LVEF greater than 40% (or shortening fraction greater than 26%) and improves with exercise OR
  • Shortening fraction greater than 26%

Pulmonary:

  • If symptomatic:
  • DLCO, FEV_1, and FEC greater than 45% predicted OR
  • Oxygen saturation greater than 85% on room air

Other:

  • Not pregnant or nursing
  • Negative pregnancy test
  • Fertile patients must use effective contraception
  • HIV negative
  • No uncontrolled viral, bacterial, or fungal infection

PRIOR CONCURRENT THERAPY:

Biologic therapy:

  • See Disease Characteristics
  • At least 1 year since prior allogeneic stem cell transplantation (SCT) with cytoreductive preparative therapy
  • At least 6 months since prior autologous SCT
  • No concurrent thrombopoietic growth factors

Chemotherapy:

  • See Disease Characteristics
  • See Biologic therapy

Endocrine therapy:

  • Not specified

Radiotherapy:

  • Not specified

Surgery:

  • Not specified

Trial locations and contacts

23 sites in 1 country.

23 sites in 1 country

United States23 sites
  • Warren Grant Magnuson Clinical Center - NCI Clinical Studies Support

    Bethesda, Maryland, 20892-1182

  • Warren Grant Magnuson Clinical Center

    Bethesda, Maryland, 20892-1182

  • Dana-Farber/Harvard Cancer Center at Dana Farber Cancer Institute

    Boston, Massachusetts, 02115

  • Cincinnati Children's Hospital Medical Center

    Cincinnati, Ohio, 45229

  • Ireland Cancer Center

    Cleveland, Ohio, 44106-5065

  • Medical City Dallas Hospital

    Dallas, Texas, 75230

  • City of Hope Comprehensive Cancer Center

    Duarte, California, 91010-3000

  • Duke Comprehensive Cancer Center

    Durham, North Carolina, 27710

  • Spectrum Health and DeVos Children's Hospital

    Grand Rapids, Michigan, 49503

  • Cancer Center at Hackensack University Medical Center

    Hackensack, New Jersey, 07601

  • Indiana University Cancer Center

    Indianapolis, Indiana, 46202-5289

  • Children's Mercy Hospital

    Kansas City, Missouri, 64108

  • Children's Hospital Los Angeles

    Los Angeles, California, 90027-0700

  • Jonsson Comprehensive Cancer Center, UCLA

    Los Angeles, California, 90095-1781

  • North Shore University Hospital

    Manhasset, New York, 11030

  • University of Minnesota Cancer Center

    Minneapolis, Minnesota, 55455

  • Children's Hospital of New Orleans

    New Orleans, Louisiana, 70118

  • Children's Hospital of Orange County

    Orange, California, 92868

  • Children's Hospital of Pittsburgh

    Pittsburgh, Pennsylvania, 15213

  • James P. Wilmot Cancer Center at University of Rochester Medical Center

    Rochester, New York, 14642

  • Fred Hutchinson Cancer Research Center

    Seattle, Washington, 98109

  • Cardinal Glennon Children's Hospital

    St Louis, Missouri, 63104

  • Children's National Medical Center

    Washington D.C., District of Columbia, 20010-2970

Other trials in United States

About this study

Official title: A Multicenter Study of Unrelated Umbilical Cord Blood as an Alternate Source of Stem Cells for Transplantation

RATIONALE: Drugs used in chemotherapy use different ways to stop cancer cells from dividing so they stop growing or die. Umbilical cord blood transplantation may be able to replace immune cells that were destroyed by the chemotherapy or radiation therapy that was used to kill cancer cells.

PURPOSE: Phase II trial to study the effectiveness of umbilical cord blood transplantation plus combination chemotherapy in treating patients who have hematologic cancer or nonmalignant hematologic disease.

Read the detailed description

OBJECTIVES:

  • Determine the efficacy of umbilical cord blood transplantation, as measured by durable neutrophil engraftment, in patients with malignant or nonmalignant hematological disease.
  • Determine the disease-free survival and long-term survival in patients treated with this regimen.
  • Determine the incidence of neutrophil engraftment, primary and secondary graft failure, platelet engraftment, and RBC engraftment in patients treated with this regimen.
  • Determine the incidence and severity of acute and chronic graft-versus-host disease, complications (infection, veno-occlusive disease, interstitial pneumonitis), relapse, other malignancies, lymphoproliferative disorders, and posttransplantation myelodysplasia in patients treated with this regimen.
  • Determine the immune reconstitution in patients treated with this regimen.

OUTLINE: This is a multicenter study. Patients are stratified according to disease group (malignant vs nonmalignant). Patients with malignant disease are further stratified according to quality of HLA match (1 or 2/6 vs 3/6 vs 4/6 vs 5/6 or 6/6), cell dose, and age.

Patients are assigned to one of three conditioning regimens, depending on disease.

  • Group A (malignant disease ): Patients undergo total body irradiation (TBI) once on day -8 and twice daily on days -7 to -4. Male patients with acute lymphocytic leukemia (ALL) undergo radiotherapy boost to testes. Patients receive cyclophosphamide (CTX) IV on days -3 and -2 and methylprednisolone (MePRDL) IV and anti-thymocyte globulin (ATG) IV on days -3 to -1.
  • Group B (inborn errors of metabolism/storage disease): Patients receive oral busulfan (BU) every 6 hours on days -6 and -5, CTX IV on days -4 and -3, and MePRDL IV and ATG IV every 12 hours on days -2 and -1.
  • Group C (other nonmalignant diseases): Patients receive oral BU every 6 hours on days -9 to -6, CTX IV on days -5 to -2, and MePRDL IV and ATG IV on days -3 to -1.

Patients in all groups receive cord blood IV over a maximum of 30 minutes on day 0. Patients also receive MePRDL IV with the first half of the infusion administered immediately before the cord blood infusion and filgrastim (G-CSF) IV beginning 4 hours after transplantation and continuing until blood counts recover.

Patients are followed at 30, 60, and 90 days; at 6 months; and then annually thereafter.

PROJECTED ACCRUAL: Approximately 390 patients will be accrued for this study within 5 years.

Being tested
anti-thymocyte globulin, filgrastim, busulfan, cyclophosphamide, methylprednisolone
Keywords
recurrent childhood acute lymphoblastic leukemia, recurrent childhood lymphoblastic lymphoma, recurrent childhood acute myeloid leukemia, relapsing chronic myelogenous leukemia, chronic phase chronic myelogenous leukemia, accelerated phase chronic myelogenous leukemia, childhood acute myeloid leukemia in remission, childhood acute lymphoblastic leukemia in remission, recurrent/refractory childhood Hodgkin lymphoma, refractory anemia, refractory anemia with ringed sideroblasts, refractory anemia with excess blasts, refractory anemia with excess blasts in transformation, chronic myelomonocytic leukemia, acute undifferentiated leukemia, secondary acute myeloid leukemia, de novo myelodysplastic syndromes, previously treated myelodysplastic syndromes, secondary myelodysplastic syndromes, recurrent childhood small noncleaved cell lymphoma
Medical subject headings
Leukemia, Lymphoma, Myelodysplastic Syndromes, Myelodysplastic-Myeloproliferative Diseases, Precursor Cell Lymphoblastic Leukemia-Lymphoma, Leukemia, Myeloid, Chronic-Phase, Leukemia, Myeloid, Accelerated Phase, Recurrence

What participants receive

What participants receive. In a randomised study each person is assigned to one group by chance.

Timeline

From the start of the study to its completion; the mark is today. Estimated dates are the sponsor’s plan.

  1. First posted27 Jan 2003 (estimated)
  2. Study startDec 1998
  3. Primary completionAug 2005
  4. Study completionAug 2005

Resources

More details

For doctors and researchers: how the study is designed, who runs it, and its registry IDs.

Study design
Study type
Interventional
Phase
Phase 2
Primary purpose
Treatment
Masking
None (open label)
Enrolment
390 participants (estimated)
IDs, dates and publications
ClinicalTrials.gov ID
NCT00003913
Sponsor's protocol ID
1330.00
Other IDs
FHCRC-1330.00, UMN-MT-9817, NCI-G99-1523, CDR0000067092
Status last verified
Mar 2010
First submitted
1 Nov 1999
Last updated
2 Apr 2010
Results posted
No

Questions about this trial

What is this clinical trial studying?

A Phase 2 study testing anti-thymocyte globulin, filgrastim and busulfan in people with Leukemia and Lymphoma, run by Fred Hutchinson Cancer Center at 23 sites in United States.

The full registered description is in the About this study section and the official record.

Who may be eligible to take part?

Eligibility is decided by the study team after screening, so read the full criteria and contact a listed site.

Is this clinical trial currently recruiting?

The record says: finished, as of the sponsor's last update on 2 Apr 2010. Status can change between updates, so confirm with the study contact before making plans.

Where is the study taking place?

The record lists 23 sites in United States. Whether a site is taking part right now should be confirmed with that site. See every site.

What are the possible benefits and risks?

They depend on the study and the treatment, and no study can promise a benefit. The study team explains the known risks during informed consent, before anyone joins; the record itself does not list them.

What does this phase mean?

Phase 2 studies give the treatment to a larger group to see whether it has the intended effect and to keep checking safety.

Not every study follows the same path, and some studies (observational studies, device studies) have no phase.

Are results available for this study?

The study is completed, but results are not available in the source record. That does not mean the treatment did or did not work.

How can a doctor refer a patient or contact the research team?

The record lists no contact. The official record names the sponsor, who can be asked directly. AzTrials does not enrol participants or take referrals.

Where can I read the original study information?
Does a listing mean the treatment is approved or proven to work?

No. A listing means the study is registered. It does not show that the treatment is safe, works, or is approved by a regulator.

How often is this information updated?

AzTrials copies changed records from ClinicalTrials.gov every night and reloads the whole registry every week. The sponsor last updated this record on 2 Apr 2010.

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